Diseases
Diseases With an Approved Gene-Editing Treatment
The conditions where gene editing has crossed from research into approved medicine.
Como esta lista é construída
Two conditions, both blood disorders, both treatable by the same intervention. That is the entire list — and understanding why it is so short tells you more about this field than any success story.
| # | Entrada | Categoria | Estado |
|---|---|---|---|
| 1 | Sickle Cell Disease An inherited blood disorder in which a single DNA letter change makes red blood cells… | Blood disorders | Approved |
| 2 | Beta Thalassemia An inherited disorder in which the body makes too little beta-globin, leaving many… | Blood disorders | Approved |
O que esta lista não dizAn approved treatment existing does not mean it is available, affordable or suitable for any particular person.