Treatments
Approved Gene-Editing Therapies
Every gene-editing medicine that a national regulator has authorised, worldwide.
Danh sách này được xây dựng như thế nào
This list is deliberately short, and its shortness is the point. Enormous scientific progress has so far produced a very small number of approved editing medicines. Everything else on this site that sounds promising is research.
| # | Mục | Danh mục | Trạng thái |
|---|---|---|---|
| 1 | Casgevy (exagamglogene autotemcel) The first CRISPR-based medicine approved anywhere in the world: a one-time therapy made… | Sickle cell disease; beta thalassemia | Approved |
| 2 | Lyfgenia (lovotibeglogene autotemcel) Approved on the same day as Casgevy for sickle cell disease, but a gene-addition therapy… | Sickle cell disease | Approved |
| 3 | Zynteglo (betibeglogene autotemcel) An approved gene-addition therapy for transfusion-dependent beta thalassemia: the… | Beta thalassemia | Approved |
Danh sách này không cho bạn biết điều gìApproval is country-specific and does not mean a treatment is available, affordable or suitable for any individual. This list includes gene-addition therapies where they are approved for the same conditions, clearly labelled, because the distinction is the point.